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Ionis Pharmaceuticals, Inc. is a biotechno … Ionis Pharmaceuticals, Inc. is a biotechnology company based in Carlsbad, California, that specializes in discovering and developing RNA-targeted therapeutics. The company has 3 commercially approved medicines: Spinraza (Nusinersen), Tegsedi (Inotersen), and Waylivra (Volanesorsen) and has 4 drugs in pivotal studies: tominersen for Huntington’s disease, tofersen for SOD1-ALS, AKCEA-APO(a)-LRx for cardiovascular disease, and AKCEA-TTR-LRx for all forms of TTR amyloidosis. The company was named Isis Pharmaceuticals until December 2015. Isis Pharmaceuticals until December 2015.
, La Ionis Pharmaceuticals (conosciuta anche … La Ionis Pharmaceuticals (conosciuta anche come Isis Pharmaceuticals fino al dicembre 2015) è un'azienda statunitense fondata nel 1989 con sede a Carlsbad, in California. L'azienda è attiva nel settore farmaceutico con più di 35 medicinali in produzione tra cui quelli per la riduzione della huntingtina (IONIS-HTTRx) nei soggetti affetti dalla malattia di Huntington e per la cura della atrofia muscolare spinale . Vengono prodotti anche farmaci per la riduzione dei livelli di colesterolo. L'azienda è stata fondata da Stanley T. Crooke, ex esponente di GlaxoSmithKline, al fine di commercializzare la .ithKline, al fine di commercializzare la .
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La Ionis Pharmaceuticals (conosciuta anche … La Ionis Pharmaceuticals (conosciuta anche come Isis Pharmaceuticals fino al dicembre 2015) è un'azienda statunitense fondata nel 1989 con sede a Carlsbad, in California. L'azienda è attiva nel settore farmaceutico con più di 35 medicinali in produzione tra cui quelli per la riduzione della huntingtina (IONIS-HTTRx) nei soggetti affetti dalla malattia di Huntington e per la cura della atrofia muscolare spinale . Vengono prodotti anche farmaci per la riduzione dei livelli di colesterolo.r la riduzione dei livelli di colesterolo.
, Ionis Pharmaceuticals, Inc. is a biotechno … Ionis Pharmaceuticals, Inc. is a biotechnology company based in Carlsbad, California, that specializes in discovering and developing RNA-targeted therapeutics. The company has 3 commercially approved medicines: Spinraza (Nusinersen), Tegsedi (Inotersen), and Waylivra (Volanesorsen) and has 4 drugs in pivotal studies: tominersen for Huntington’s disease, tofersen for SOD1-ALS, AKCEA-APO(a)-LRx for cardiovascular disease, and AKCEA-TTR-LRx for all forms of TTR amyloidosis. The company was named Isis Pharmaceuticals until December 2015. Isis Pharmaceuticals until December 2015.
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Ionis Pharmaceuticals
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